For patients diagnosed with rare diseases like hemophilia and muscular dystrophy, treatment has historically been difficult and the prognoses terminal. But the advent of new cell and gene therapies are providing hope, as they fight the root cause of disease [See the full post…]

David Altshuler was living the academic dream as professor and human geneticist at Harvard and MIT, where he was co-founder and Deputy Director of the Broad Institute.  Yet in December 2014, he left this life to join Vertex, in continued [See the full post…]